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在当今基因干预和基因治疗领域里,有两项极为引人注目的技术,那就是反义核酸技术和ribozyme技术。而二者的完美结合,则成为基因治疗的强劲武器。本文对目前已经发现的ribozyme作了简要介绍,并描绘了这一武器在现代基因干预和基因治疗中的应用现状和应用前景。
In today’s field of gene intervention and gene therapy, there are two extremely compelling technologies that are antisense and ribozyme technologies. The perfect combination of the two is a powerful weapon for gene therapy. In this paper, we briefly introduced the ribozyme that we have discovered so far, and described the present situation and the application prospect of this weapon in the modern gene intervention and gene therapy.