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通过改变病人基因治疗某些遗传病,似乎不象人们通常认为的那样需要长远的时间了。今年4月份在纽约召开的“美国科学和卫生研讨会”上,“美国心脏与血液研究所”的Ja-mes Zwiebel报告了上述研究领域的研究工作。对严重合并免疫缺陷综合征的治疗正进行研究。此病罕见,但可致命,为不治之症.此病为基因治疗的对象,因为此病是由于缺少一个单基因,即为腺嘌呤核苷脱氨酶(ADA)编码的基因.疗法是用含有为ADA酶基因编码的基因工程细胞更换患者骨髓细胞.Zwie-bel研究小组使用一部分逆转录病毒DNA构成
It does not seem to take long as people generally believe to do by changing the genetics of a patient to treat certain genetic diseases. Ja-mes Zwiebel of the American Heart & Blood Institute at the American Science and Health Symposium held in New York City in April this year reported the research work in the above fields. Treatment of severe combined immunodeficiency syndrome is being studied. The disease is rare but fatal and is incurable.The disease is the target of gene therapy because the disease is due to the absence of a single gene that is the gene encoded by adenosine deaminase (ADA) Containing bone marrow cells from genetically engineered cells coded for the ADA enzyme gene.Zwie-bel’s team used a subset of retroviral DNA