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siRNA的化学修饰及靶向转运策略已广泛应用于肿瘤、病毒感染性疾病及代谢性疾病的临床治疗研究,并取得一定的进展。本文主要对siRNA的化学修饰、细胞穿透性多肽、靶向性配体及纳米颗粒等方面的研究进展作一综述。
siRNA chemical modification and targeted transport strategy has been widely used in cancer, viral infectious diseases and metabolic disease clinical research and made some progress. This article mainly reviews the research progress of chemical modification of siRNA, cell penetrating peptides, targeting ligands and nanoparticles.